Cryo-EM Captures CRISPR-Cas9 Base Editor in Action
Researchers have obtained the first 3D structure of CRISPR-Cas9 base editor which may lead to more versatility and control for use in patients.
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Workflow design and data management are pivotal components of cell and gene therapy research and development. Advances in artificial intelligence, informatics, and automation have made…
ASO Therapy Repairs Neurons from Timothy Syndrome Patients
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Epigenetic Technologies Find Clinical Applications
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Artificial cells built with dynamically reconfigurable peptide-DNA cytoskeletons demonstrate tunable functionality.
Immune Cells Stay on Standby to Defend Immune System
Defense cells are constantly stimulated by healthy tissue to keep them vigilant and ready to respond to pathogens.
Alzheimer’s Disease Neurons Reenter Cell Cycle, Become Senescent
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Immune Cells Stay on Standby to Defend Immune System
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Gene therapy has undergone a renaissance in recent years, with several drugs offering beneficial, even life-saving treatments, now approved by the FDA. One example was…